ASO therapy
Hope placed on gene therapy for rare CAMK2 syndrome
Pediatrician Daniëlle Veenma and neuroscientist Geeske van Woerden are collaborating on a treatment for the rare CAMK2 syndrome. Currently, a cure is not possible. With funding from the Dutch Hersenstichting, they are mapping out the potential of a form of gene therapy. ‘We have good hope that we will succeed.’