ACE lecture

Gene therapy for hemophilia: a cure for the royal disease?

Already 20 years ago, the first study on gene therapy for the bleeding disorder hemophilia B was published. Internist-hematologist Prof Dr Frank Leebeek explains what has happened since then. Is gene therapy the cure for the royal disease?

Reading time < 1 min

In this webinar Prof Frank Leebeek reports the latest results on efficacy, side effects, and hurdles of gene therapy for hemophilia A and B.

Academic Centers of Excellence

This video is part of a series of online lectures about the Erasmus MC Academic Centers of Excellence. Prof Frank Leebeek is affiliated with the Academic Center for Breast Cancer.

Also read